# $3.5-Million Hemophilia Gene Therapy Is World’s Most Expensive Drug

- Link: https://www.widthness.com/3-5-million-hemophilia-gene-therapy-is-worlds-most-expensive-drug/
- Published: 2022-12-12T09:00:50-06:00
- Author: Curated by John Wysocki

Image caption: Haemophilia is a genetic condition that affects the formation of blood clots (pictured). Image credit: Micro Discovery / Getty Images. Article by Miryam Naddaf. Scientific American – December 9, 2022. Originally published in Nature – December 6, 2022. On 22 November, the US Food and Drug Administration (FDA) approved the first gene therapy for the genetic blood-clotting disorder haemophilia B—a one-time treatment that costs US$3.5 million. Hemgenix—developed by the pharmaceutical company CSL Behring, based in King of Prussia, Pennsylvania—uses a modified virus to deliver a gene to the recipient’s liver cells. […] Click here to view original web page at www.scientificamerican.com