US regulators approve two gene therapies for sickle cell disease

Image caption: A blood cell altered by sickle cell disease. Image credit: AP. Article by Edward Helmore. The Guardian – December 8, 2023.

The US Food and Drug Administration has approved a pair of gene therapies for sickle cell disease, including the first treatment based on the breakthrough Crispr gene-editing technology, opening up two “transformative therapy” avenues for some patients. The FDA […]

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