First gene therapy for deadly form of muscular dystrophy gets FDA approval for young children

Photo caption – File photo: Signage is seen outside of the Food and Drug Administration (FDA) headquarters in White Oak, Maryland, U.S., August 29, 2020. Reuters / Andrew Kelly / File Photo. Article by Matthew Perrone, Associated Press. PBS NewsHour – June 22, 2023.

WASHINGTON (AP) — The first gene therapy for a deadly form of muscular dystrophy received preliminary U.S. approval on Thursday despite concerns from some government scientists about the treatment’s ability to help boys with the inherited disease. The Food and Drug Administration approval provides a new option for some […]

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