The FDA just approved rub-on gene therapy that helps “butterfly” children

Photo caption: Anthony Vento with his mother and father. His skin disease is being treated with a newly approved gene therapy. Photo courtesy of Yunielkys Carvajal. Article by Antonio Regalado. MIT Technology Review – May 19, 2023.

Antonio Vento is 13 years old. He’s a tiny figure in bandages who doesn’t walk and, until recently, couldn’t see more than shadows. He has dystrophic epidermolysis bullosa, an inherited disease that makes his skin so fragile that kids with the illness are called “butterfly children.” […]

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